So for all the good the drug is doing for Luke, the results of the adolesscent double blind trial is dismal: the placebo group did as well as the group taking the drug. This is the same result Novartis got from the adult trial.
How can a drug have such incredible results (reversing Fragile X!!!) in animal studies and be such a wash-out in humans???
I am brokenhearted, but not beaten. Mt Sinai is conducting a study on another drug…..